Search for Clinical Trial Results

Muscular Dystrophy, Oculopharyngeal - 9 Studies Found
Status | Study |
Completed |
Study Name: Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts Condition: Muscular Dystrophy, Oculopharyngeal Date: 2008-10-15 Interventions: Procedure: Autologous myoblasts transplantation and myotomy Graft of autologous cell muscles (myoblasts) |
Recruiting |
Study Name: Screening in Oculopharyngeal Muscular Dystrophy Condition: Oculopharyngeal Muscular Dystrophy Date: 2016-08-19 Interventions:
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Not yet recruiting |
Study Name: Natural History Study of Oculopharyngeal Muscular Dystrophy Condition: Oculopharyngeal Muscular Dystrophy Date: 2017-05-16 Interventions: Other: Non-interventional study Non-interventional study |
Not yet recruiting |
Study Name: Effect of Aerobic Training in Patients With Oculopharyngeal Muscular Dystrophy Condition: Oculopharyngeal Muscular Dystrophy Date: 2014-06-04 Interventions: Behavioral: Exercise Ten weeks of home-training on a cycle ergometer 3 times a week for 30 minutes. |
Active, not recruiting |
Study Name: Continuation Protocol to Protocol BBCO-001 Condition: Muscular Dystrophy, Oculopharyngeal (OPMD) Date: 2014-12-25 Interventions: Drug: Cabaletta 30gr Cabaletta 30 g for IV infusion administered every week over an additional 52 weeks |
Completed |
Study Name: Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients Condition: Oculopharyngeal Muscular Dystrophy Date: 2013-12-08 Interventions: Drug: Cabaletta |
Active, not recruiting |
Study Name: Treatment of Ptosis to Muscular Dystrophy Oculopharyngeal by Myoblast Autologous Graft Condition:
Date: 2016-03-08 Interventions: Biological: Myoblast autologous graft 30 million autologous myoblasts in 6 intramuscular injections No t |
Completed |
Study Name: Study of Muscle Abnormalities in Patients With Specific Genetic Mutations Condition:
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Completed |
Study Name: Dysphagia in Oculopharyngeal Muscular Dystrophy (OPMD)- Evaluation, Endoscopic Examination of Swallowing, Treatment and Long Term Follow up Condition: Dysphagia Date: 2010-07-21 Interventions: Procedure: Upper esophageal sphincter myotomy Upper esophageal sphincter release operation to allow bett |