Search for Clinical Trial Results

Lysosomal Storage Diseases - 50 Studies Found
Status | Study |
Recruiting |
Study Name: Molecular and Cellular Mechanisms of Lysosomal Storage Diseases Condition: Lysosomal Storage Disorders Date: 2013-11-25 |
Withdrawn |
Study Name: Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases Condition:
Interventions: Biological: ALD-601 ALD-601 is manufactured by Aldagen from the 20% compartment of the selected umbilica |
Enrolling by invitation |
Study Name: Genetic Studies of Lysosomal Storage Disorders Condition:
Date: 1999-11-03 |
Completed |
Study Name: The Classification and Cause of Leukodystrophies of Unknown Cause Condition: Lysosomal Storage Disease Date: 1999-11-03 |
Active, not recruiting |
Study Name: Gene Therapy for Metachromatic Leukodystrophy Condition: Lysosomal Storage Disease Date: 2012-03-16 Interventions: Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Recruiting |
Study Name: Biomarker for Krabbe Disease Condition:
Date: 2011-08-29 |
Recruiting |
Study Name: Biomarker for Pompe Disease Condition:
Date: 2011-10-21 |
Recruiting |
Study Name: Biomarker for Maroteaux-Lamy Disease Condition:
Date: 2011-10-24 |
Recruiting |
Study Name: Biomarker for Morquio Disease Condition:
Date: 2011-10-21 |
Completed |
Study Name: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders Condition:
Date: 2012-06-20 Interventions:
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