Leukodystrophy - 153 Studies Found
Completed |
: The Natural History of Infantile Globoid Cell Leukodystrophy : Infantile Globoid Cell Leukodystrophy : 2009-09-23 |
Completed |
: Long-term Metazym Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) : Late Infantile Metachromatic Leukodystrophy : 2008-02-29 : Biological: Recombinant human Arylsulfatase A (rhASA) intravenous infusion, every other week for 26 week |
Completed |
: Imaging Study of the White Matter Lesions in Children With Metachromatic Leucodystrophy : Late Infantile Metachromatic Leukodystrophy : 2011-03-09 : Other: High-field MRI (3 Teslas) |
Enrolling by invitation |
: Open-Label Extension Study Evaluating Safety and Efficacy of HGT-1110 in Patients With Metachromatic Leukodystrophy : Metachromatic Leukodystrophy (MLD) : 2013-06-20 :
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Completed |
: Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) : Metachromatic Leukodystrophy (MLD) : 2007-01-04 : Drug: rhASA intravenous infusion 25 U/kg,50 U/kg, 100U/kg or 200 U/kg every other week for 26 weeks |
Recruiting |
: Natural History of the Leukodystrophies : Leukodystrophies : 2016-04-07 |
Completed |
: Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation : Metachromatic Leukodystrophy : 2011-02-23 : Drug: rhARSA intravenous infusion 100U/kg every other week for 18 months |
Terminated |
: Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD : Late Infantile Metachromatic Leukodystrophy : 2008-05-19 : Drug: HGT-1111 Patients currently dosed with 100 U/kg or 200 U/kg will continue this treatment. Patients |
Recruiting |
: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy :
: 2015-08-12 : Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
Recruiting |
: The Nosology and Etiology of Leukodystrophies of Unknown Causes :
: 2009-04-25 |