Lysosomal Storage Diseases - 50 Studies Found
Enrolling by invitation |
: An MRI Study on Muscular Diseases -Pompe Disease and Dystrophia Myotonica- :
: 2015-12-08 |
Active, not recruiting |
: First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221 : Pompe Disease : 2016-01-26 :
|
Recruiting |
: Safety and Effectiveness of Resistance Exercise Training in Patients With Pompe Disease. :
: 2015-12-10 : Other: Resistance Exercise Training Resistance Exercise Tr |
Not yet recruiting |
: Prevalence of Pompe's Disease in Respiratory Clinics : Pompe's Disease : 2015-08-17 : Other: Prospective observational study Prospective observational study collecting data during a clinic v |
Recruiting |
: Immune Modulation Therapy for Pompe Disease : Pompe Disease : 2015-08-10 :
|
Recruiting |
: LYSO-PROVE - Determine the Prognostic Value of Lyso-Gb1 for Monitoring the Progress of Gaucher Disease :
|
Recruiting |
: CPAP for Infantile Pompe Disease : Pompe Disease : 2015-03-21 : Procedure: continuous positive airway pressure CPAP training for muscle strength |
Completed |
: Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease : Pompe Disease : 2015-03-22 : Drug: Salbutamol |
Recruiting |
: A Long-term Study for the Outcome of Pompe Disease : Pompe Disease : 2015-03-21 |
Not yet recruiting |
: Diet and Exercise in Pompe Disease :
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