Refsum Disease - 13 Studies Found
Completed |
: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid :
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Completed |
: Betaine and Peroxisome Biogenesis Disorders : Peroxisome Biogenesis Disorders : 2013-03-29 : Drug: Betaine Betaine will be given orally (mixed with foo |