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Pyruvate Kinase Deficiency - 2 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: A Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency Condición: Pyruvate Kinase Deficiency Fecha: 2015-06-10 Intervenciones: Drug: AG-348 A range of doses of AG-348 will be tested based on the assessment of safety, tolerability a |
Active, not recruiting |
Nombre del estudio: Pyruvate Kinase Deficiency Natural History Study Condición:
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